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Webcast

What if eCOA could elevate your next rare disease trial?

Interview with Prof. Olivier Blin, Professor of Pharmacology, rare disease expert, and Orphan Dev coordinator Despite remarkable progress in rare disease research, 90% of rare diseases still lack an approved treatment....

White Paper

Elevating rare disease clinical trials through eCOA – From patient voice to regulatory success

Rare disease

Rare disease clinical trials face a unique combination of scientific, operational, and regulatory challenges. Small patient populations, heterogeneous disease presentation,...

Article

Overcoming rare disease trial challenges: the strategic impact of eCOA

Rare disease

Rare disease trials are crucial for addressing major unmet medical needs, yet they are among the most challenging to design...

Article

Rare disease clinical research: it is time to tackle what matters most to patients

Rare disease

Supporting the development and evaluation of new treatments for rare diseases has become a key priority of the 21st century....

Webcast

Working with patient associations: What is the key to a positive interaction?

Patients insights Rare disease

What rare disease patients and families want is a simpler life.Discover here what makes the relationship between the members of...

Webcast

How a patient association gave rise to a company

Patients insights Rare disease

A patient association in rare diseases is first and foremost families who all have one thing in common: they need...

Case study

Rare Disease case study

Rare disease

Over 90% of rare diseases have no treatment… There are more than 6,000 known rare diseases... Approximately 80% of them have...

Digitalization Trends in Tackling the Complexity of Clinical Trials for Patients with Multiple Health Conditions

Rare disease

Patients participating in clinical research face a whole range of challenges, and it is particularly worse for those living with...

Article

Partnering with patients to boost clinical research in rare diseases

Patients insights Rare disease

Although much progress has been made in developing scientific knowledge and conducting clinical research in rare diseases, serious challenges remain....

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Rare disease

What if eCOA could elevate your next rare disease trial?

Elevating rare disease clinical trials through eCOA – From patient voice to regulatory success

Overcoming rare disease trial challenges: the strategic impact of eCOA

Rare disease clinical research: it is time to tackle what matters most to patients

Working with patient associations: What is the key to a positive interaction?

How a patient association gave rise to a company

Rare Disease case study

Digitalization Trends in Tackling the Complexity of Clinical Trials for Patients with Multiple Health Conditions

Partnering with patients to boost clinical research in rare diseases

What if eCOA could elevate your next rare disease trial?

Elevating rare disease clinical trials through eCOA – From patient...

Overcoming rare disease trial challenges: the strategic impact of eCOA

Kayentis and Perceptive eClinical partner to tackle increasing digital system...

Raising the bar again: Kayentis achieves 95.9% client Recommendation Rate...

Kayentis and Ametris join forces to deliver integrated eCOA solution...

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